Genetic Target for Treating Duchenne Muscular Dystrophy Identified
Researchers have linked the Jagged1 gene to a much milder form of muscular dystrophy in golden retrievers.
Researchers have linked the Jagged1 gene to a much milder form of muscular dystrophy in golden retrievers.
The FDA is set to make a decision on the NDA by late February, 2016.
A deflazacort regimen appeared to slow loss of ambulation, but not without several side effects.
The conditions are similar, but differ in rate of progression and age of onset.